Heredodegenerative Disorders, Nervous System - 25 Studies Found
Active, not recruiting |
: A Multicenter, Multinational, Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease :
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Completed |
: Neuronal Ceroid Lipofuscinosis and Associated Sleep Abnormalities :
: 2013-09-25 |
Completed |
: A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Efficacy of Intracerebroventricular BMN 190 in Patients With Late-Infantile Neuronal Ceroid Lipofuscinosis (CLN2) Disease :
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Recruiting |
: Clinical and Neuropsychological Investigations in Batten Disease : Neuronal Ceroid Lipofuscinosis : 2013-05-17 |
Terminated |
: Collection of Cerebrospinal Fluid in Healthy Children :
: 2012-08-15 : Other: Group 1 Collecting a small amount of cerebrospinal fluid (5 mL) from healthy children, ages 2 yrs |
Recruiting |
: AAVRh.10 Administered to Children With Late Infantile Neuronal Ceroid Lipofuscinosis :
: 2010-12-13 : Biological: AAVrh.10CUCLN2 There will be 2 dose cohorts in this study. Group A consists of 2 subjects wh |
Completed |
: Cellcept for Treatment of Juvenile Neuronal Ceroid Lipofuscinosis : Juvenile Neuronal Ceroid Lipofuscinosis : 2011-07-05 :
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Withdrawn |
: Safety and Efficacy Study of HuCNS-SC in Subjects With Neuronal Ceroid Lipofuscinosis : Neuronal Ceroid Lipofuscinosis : 2010-11-05 : Biological: HuCNS-SC Surgery to implant human CNS stem cells |
Recruiting |
: Safety Study of a Gene Transfer Vector (Rh.10) for Children With Late Infantile Neuronal Ceroid Lipofuscinosis :
: 2010-03-22 :
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Recruiting |
: Genotype-Phenotype Correlations of Late Infantile Neuronal Ceroid Lipofuscinosis :
: 2009-12-16 |